Research output per year
Research output per year
- 1 results
Search results
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2025
Real-world evidence for Pompe disease remains fragmented. Comment on “A rare partnership: patient community and industry collaboration to shape the impact of real-world evidence on the rare disease ecosystem” by Klein et al.
Kruijshaar, M. E., House, T., Schoser, B., Laforêt, P., Theunissen, M. T. M., Wenninger, S., Hundsberger, T., Diaz-Manera, J., van der Ploeg, A. T. & van der Beek, N. A. M. E., 14 Feb 2025, In: Orphanet Journal of Rare Diseases. 20, 1, 74.Research output: Contribution to journal › Comment/Letter to the editor › Academic › peer-review
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