A Clinical Trial of Gene Therapy for Mucopolysaccharidosis VI, a Severe Lysosomal Storage Disorder (MeuSIX)

A Auricchio, K Kozarsky, M Audit, G Andria, S Sivri, Ans van der Ploeg, MG Valsecchi, F Incardona

Research output: Contribution to journalArticleAcademicpeer-review

Original languageUndefined/Unknown
Pages (from-to)86-88
Number of pages3
JournalHuman gene therapy clinical development
Volume26
Issue number2
DOIs
Publication statusPublished - 2015

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