A randomized study of alglucosidase alfa in late-onset Pompe's disease

Ans van der Ploeg, PR Clemens, D Corzo, DM Escolar, J Florence, GJ Groeneveld, S Herson, PS Kishnani, P Laforet, S Lake, DJ Lange, RT Leshner, C Morgan, K Nozaki, DJ Park, A Pestronk, B Rosenbloom, A Skrinar, Carine Capelle, N.A.M.E. van der BeekM Wasserstein, SA Zivkovic

Research output: Contribution to journalArticleAcademicpeer-review

631 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)1396-1406
Number of pages11
JournalNew England Journal of Medicine
Volume362
DOIs
Publication statusPublished - 2010

Research programs

  • EMC MM-01-54-01
  • EMC MM-04-44-02

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