Adenovirus-mediated transfer of the acid alpha-glucosidase gene into fibroblasts, myoblasts and myotubes from patients with glycogen storage disease type II leads to high level expression of enzyme and corrects glycogen accumulation

MP Nicolino, J-P Puech, EJ Kremer, Arnold Reuser, C Mbebi, M Verdière-Sahuque, A Kahn, L Poenaru

Research output: Contribution to journalArticleAcademicpeer-review

42 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)1695-1702
Number of pages8
JournalHuman Molecular Genetics
Volume7
Issue number11
DOIs
Publication statusPublished - 1998

Research programs

  • EMC MGC-02-96-01

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