Antisense Oligonucleotide-Based Splicing Correction in Individuals with Leber Congenital Amaurosis due to Compound Heterozygosity for the c.2991+1655A > G Mutation in CEP290

L Duijkers, LI van den Born, J Neidhardt, NMA Bax, Laurence Pierrache, BJ Klevering, RWJ Collin, A Garanto

Research output: Contribution to journalArticleAcademicpeer-review

22 Citations (Scopus)
6 Downloads (Pure)
Original languageUndefined/Unknown
Article number753
JournalInternational Journal of Molecular Sciences
Issue number3
Publication statusPublished - 2018

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