Antisense Oligonucleotides Promote Exon Inclusion and Correct the Common c.-32-13T > G GAA Splicing Variant in Pompe Disease

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Original language	Undefined/Unknown
Pages (from-to)	90-100
Number of pages	11
Journal	Molecular therapy. Nucleic acids
Volume	7
DOIs	https://doi.org/10.1016/j.omtn.2017.03.001
Publication status	Published - 2017

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title = "Antisense Oligonucleotides Promote Exon Inclusion and Correct the Common c.-32-13T > G GAA Splicing Variant in Pompe Disease",

author = "Erik Wal and Atze Bergsma and Joon Pijnenburg and {van der Ploeg}, Ans and Pim Pijnappel",

year = "2017",

doi = "10.1016/j.omtn.2017.03.001",

language = "Undefined/Unknown",

volume = "7",

pages = "90--100",

journal = "Molecular therapy. Nucleic acids",

issn = "2162-2531",

publisher = "Cell Press",

}

TY - JOUR

T1 - Antisense Oligonucleotides Promote Exon Inclusion and Correct the Common c.-32-13T > G GAA Splicing Variant in Pompe Disease

AU - Wal, Erik

AU - Bergsma, Atze

AU - Pijnenburg, Joon

AU - van der Ploeg, Ans

AU - Pijnappel, Pim

PY - 2017

Y1 - 2017

U2 - 10.1016/j.omtn.2017.03.001

DO - 10.1016/j.omtn.2017.03.001

M3 - Article

C2 - 28624228

SN - 2162-2531

VL - 7

SP - 90

EP - 100

JO - Molecular therapy. Nucleic acids

JF - Molecular therapy. Nucleic acids

ER -