Availability, accessibility and delivery to patients of the 28 orphan medicines approved by the European Medicine Agency for hereditary metabolic diseases in the MetabERN network

JM Heard; C Vrinten; M Schlander; CM Bellettato; C Lingen; M Scarpa; Hidde Huidekoper; U Groselj; MZ Tansek

doi:10.1186/s13023-019-1280-5

Availability, accessibility and delivery to patients of the 28 orphan medicines approved by the European Medicine Agency for hereditary metabolic diseases in the MetabERN network

JM Heard, C Vrinten, M Schlander, CM Bellettato, C Lingen, M Scarpa, Hidde Huidekoper, U Groselj, MZ Tansek

Pediatrics

Research output: Contribution to journal › Article › Academic › peer-review

7 Citations (Scopus)

Original language	Undefined/Unknown
Article number	3
Journal	Orphanet Journal of Rare Diseases
Volume	15
Issue number	1
DOIs	https://doi.org/10.1186/s13023-019-1280-5
Publication status	Published - 2020

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10.1186/s13023-019-1280-5

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Heard, JM., Vrinten, C., Schlander, M., Bellettato, CM., Lingen, C., Scarpa, M., Huidekoper, H., Groselj, U., & Tansek, MZ. (2020). Availability, accessibility and delivery to patients of the 28 orphan medicines approved by the European Medicine Agency for hereditary metabolic diseases in the MetabERN network. Orphanet Journal of Rare Diseases, 15(1), [3]. https://doi.org/10.1186/s13023-019-1280-5

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Heard, JM, Vrinten, C, Schlander, M, Bellettato, CM, Lingen, C, Scarpa, M, Huidekoper, H, Groselj, U & Tansek, MZ 2020, 'Availability, accessibility and delivery to patients of the 28 orphan medicines approved by the European Medicine Agency for hereditary metabolic diseases in the MetabERN network', Orphanet Journal of Rare Diseases, vol. 15, no. 1, 3. https://doi.org/10.1186/s13023-019-1280-5

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T1 - Availability, accessibility and delivery to patients of the 28 orphan medicines approved by the European Medicine Agency for hereditary metabolic diseases in the MetabERN network

AU - Heard, JM

AU - Vrinten, C

AU - Schlander, M

AU - Bellettato, CM

AU - Lingen, C

AU - Scarpa, M

AU - Huidekoper, Hidde

AU - Groselj, U

AU - Tansek, MZ

PY - 2020

Y1 - 2020

U2 - 10.1186/s13023-019-1280-5

DO - 10.1186/s13023-019-1280-5

M3 - Article

VL - 15

JO - Orphanet Journal of Rare Diseases

JF - Orphanet Journal of Rare Diseases

SN - 1750-1172

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M1 - 3

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