Cardiovascular abnormalities in late-onset Pompe disease and response to enzyme replacement therapy

D Forsha, JS Li, B Smith, Ans van der Ploeg, P Kishnani, SK Pasquali

Research output: Contribution to journalArticleAcademicpeer-review

43 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)625-631
Number of pages7
JournalGenetics in Medicine
Volume13
Issue number7
DOIs
Publication statusPublished - 2011

Research programs

  • EMC MM-01-54-01

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