Chemical chaperones improve transport and enhance stability of mutant alfa-glucosidases in glycogen storage disease type II

T Okumiya, Marian Haan, L van Vliet, H Takeuchi, Ans van der Ploeg, Arnold Reuser

Research output: Contribution to journalArticleAcademicpeer-review

93 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)49-57
Number of pages9
JournalMolecular Genetics and Metabolism
Volume90
DOIs
Publication statusPublished - 2007

Research programs

  • EMC MGC-02-96-01
  • EMC MM-01-54-01

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