Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease

Research output: Contribution to journalArticleAcademicpeer-review

21 Citations (Scopus)
15 Downloads (Pure)
Original languageEnglish
Article number75
Pages (from-to)75
JournalOrphanet Journal of Rare Diseases
Volume9
DOIs
Publication statusPublished - 2014

Research programs

  • EMC NIHES-05-63-02 Quality
  • EMC MM-01-54-01

Cite this