CRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid Biobank

MH Geurts, E van de Poel, GD Amatngalim, R Oka, FM Meijers, E Kruisselbrink, P van Mourik, G Berkers, KM de Winter-de Groot, S Michel, Danya Muilwijk, BL Aalbers, J Mullenders, SF Boj, SWF Suen, JE Brunsveld, Hettie Janssens, MA Mall, SY Graeber, R van BoxtelCK van der Ent, JM Beekman, H Clevers

Research output: Contribution to journalArticleAcademicpeer-review

154 Citations (Scopus)
Original languageEnglish
Pages (from-to)503-510
Number of pages8
JournalCell Stem Cell
Volume26
Issue number4
DOIs
Publication statusPublished - 2020

Research programs

  • EMC ONWAR-01-58-02
  • EMC OR-01-54-02

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