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CRISPR-Based Adenine Editors Correct Nonsense Mutations in a Cystic Fibrosis Organoid Biobank

  • MH Geurts
  • , E van de Poel
  • , GD Amatngalim
  • , R Oka
  • , FM Meijers
  • , E Kruisselbrink
  • , P van Mourik
  • , G Berkers
  • , KM de Winter-de Groot
  • , S Michel
  • , Danya Muilwijk
  • , BL Aalbers
  • , J Mullenders
  • , SF Boj
  • , SWF Suen
  • , JE Brunsveld
  • , Hettie Janssens
  • , MA Mall
  • , SY Graeber
  • , R van Boxtel
  • CK van der Ent, JM Beekman, H Clevers

Research output: Contribution to journalArticleAcademicpeer-review

201 Citations (Scopus)
Original languageEnglish
Pages (from-to)503-510
Number of pages8
JournalCell Stem Cell
Volume26
Issue number4
DOIs
Publication statusPublished - 2020

Research programs

  • EMC ONWAR-01-58-02
  • EMC OR-01-54-02

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