Original language | English |
---|---|
Article number | 247 |
Journal | Orphanet Journal of Rare Diseases |
Volume | 15 |
Issue number | 1 |
DOIs | |
Publication status | Published - 2020 |
Distal muscle weakness is a common and early feature in long-term enzyme-treated classic infantile Pompe patients
Jeroen van den Dorpel, E Poelman, Laurike Harlaar, Harmke van Kooten, Lianne van der Giessen, Pieter van Doorn, Ans van der Ploeg, Hannerieke van den Hout, N.A.M.E. van der Beek
Research output: Contribution to journal › Article › Academic › peer-review
7
Citations
(Scopus)
5
Downloads
(Pure)