Effect of enzyme therapy and prognostic factors in 69 adults with Pompe disaese: an open-label single-center study

Juna de Vries, N.A.M.E. van der Beek, Hop, Francois Karstens, JHJ Wokke, M de Visser, BGM van Engelen, JBM Kuks, AJ van der Kooi, NC Notermans, CG Faber, JJGM Verschuuren, ME Kruijshaar, Arnold Reuser, Pieter van Doorn, Ans van der Ploeg

Research output: Contribution to journalArticleAcademicpeer-review

86 Citations (Scopus)
32 Downloads (Pure)
Original languageUndefined/Unknown
Pages (from-to)73
JournalOrphanet Journal of Rare Diseases
Volume7
DOIs
Publication statusPublished - 2012

Research programs

  • EMC MGC-02-96-01
  • EMC MM-01-54-01
  • EMC MM-04-44-02
  • EMC NIHES-01-66-01

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