Effect of enzyme therapy in juvenile patients with Pompe disease: a three-year open-label study

Carine Capelle, N.A.M.E. van der Beek, Marloes Hagemans, WFM Arts, Hop, P Lee, J Jaeken, Ingrid Mulder, PJFM Merkus, D Corzo, AC Puga, Arnold Reuser, Ans van der Ploeg

Research output: Contribution to journalArticleAcademicpeer-review

58 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)775-782
Number of pages8
JournalNeuromuscular Disorders
Volume20
DOIs
Publication statusPublished - 2010

Research programs

  • EMC COEUR-09
  • EMC MGC-02-96-01
  • EMC MM-01-54-01
  • EMC MM-04-44-02
  • EMC NIHES-01-66-01
  • EMC OR-01-54-02

Cite this