Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study

Carin Gelder; Esther Poelman; Iris Plug; Marianne Hoogeveen - Westerveld; N.A.M.E. van der Beek; Arnold Reuser; Ans van der Ploeg

doi:10.1007/s10545-015-9912-y

Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study

Carin Gelder, Esther Poelman, Iris Plug, Marianne Hoogeveen - Westerveld, N.A.M.E. van der Beek, Arnold Reuser, Ans van der Ploeg

Research output: Contribution to journal › Article › Academic › peer-review

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Original language	Undefined/Unknown
Pages (from-to)	383-390
Number of pages	8
Journal	Journal of Inherited Metabolic Disease
Volume	39
Issue number	3
DOIs	https://doi.org/10.1007/s10545-015-9912-y
Publication status	Published - 2016

Research programs

EMC MM-01-54-01
EMC MM-04-44-02

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10.1007/s10545-015-9912-y

REPUB_89594-OA.pdfFinal published version, 379 KB
REPUB_89594-OA.pdfFinal published version, 379 KB

Cite this

Gelder, C., Poelman, E., Plug, I., Hoogeveen - Westerveld, M., van der Beek, N. A. M. E., Reuser, A., & van der Ploeg, A. (2016). Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study. Journal of Inherited Metabolic Disease, 39(3), 383-390. https://doi.org/10.1007/s10545-015-9912-y

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author = "Carin Gelder and Esther Poelman and Iris Plug and {Hoogeveen - Westerveld}, Marianne and {van der Beek}, N.A.M.E. and Arnold Reuser and {van der Ploeg}, Ans",

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doi = "10.1007/s10545-015-9912-y",

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Gelder, C, Poelman, E, Plug, I, Hoogeveen - Westerveld, M , van der Beek, NAME , Reuser, A & van der Ploeg, A 2016, 'Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study', Journal of Inherited Metabolic Disease, vol. 39, no. 3, pp. 383-390. https://doi.org/10.1007/s10545-015-9912-y

Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study. / Gelder, Carin; Poelman, Esther; Plug, Iris et al.
In: Journal of Inherited Metabolic Disease, Vol. 39, No. 3, 2016, p. 383-390.

Research output: Contribution to journal › Article › Academic › peer-review

TY - JOUR

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AU - Gelder, Carin

AU - Poelman, Esther

AU - Plug, Iris

AU - Hoogeveen - Westerveld, Marianne

AU - van der Beek, N.A.M.E.

AU - Reuser, Arnold

AU - van der Ploeg, Ans

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