Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study

Carin Gelder; Esther Poelman; Iris Plug; Marianne Hoogeveen - Westerveld; N.A.M.E. van der Beek; Arnold Reuser; Ans van der Ploeg

doi:10.1007/s10545-015-9912-y

Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study

Carin Gelder
, Esther Poelman
, Iris Plug
, Marianne Hoogeveen - Westerveld
, N.A.M.E. van der Beek
, Arnold Reuser
, Ans van der Ploeg

Research output: Contribution to journal › Article › Academic › peer-review

70 Citations (Scopus)

82 Downloads (Pure)

Original language	Undefined/Unknown
Pages (from-to)	383-390
Number of pages	8
Journal	Journal of Inherited Metabolic Disease
Volume	39
Issue number	3
DOIs	https://doi.org/10.1007/s10545-015-9912-y
Publication status	Published - 2016

Research programs

EMC MM-01-54-01
EMC MM-04-44-02

Access to Document

10.1007/s10545-015-9912-y

REPUB_89594-OA.pdfFinal published version, 379 KB
REPUB_89594-OA.pdfFinal published version, 379 KB

Cite this

Gelder, C., Poelman, E., Plug, I., Hoogeveen - Westerveld, M., van der Beek, N. A. M. E., Reuser, A., & van der Ploeg, A. (2016). Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study. Journal of Inherited Metabolic Disease, 39(3), 383-390. https://doi.org/10.1007/s10545-015-9912-y

@article{711b19be7fc749cdb215ad035aa3da4a,

title = "Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study",

author = "Carin Gelder and Esther Poelman and Iris Plug and \{Hoogeveen - Westerveld\}, Marianne and \{van der Beek\}, N.A.M.E. and Arnold Reuser and \{van der Ploeg\}, Ans",

year = "2016",

doi = "10.1007/s10545-015-9912-y",

language = "Undefined/Unknown",

volume = "39",

pages = "383--390",

journal = "Journal of Inherited Metabolic Disease",

issn = "0141-8955",

publisher = "Springer Netherlands",

number = "3",

}

Gelder, C, Poelman, E, Plug, I, Hoogeveen - Westerveld, M , van der Beek, NAME , Reuser, A & van der Ploeg, A 2016, 'Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study', Journal of Inherited Metabolic Disease, vol. 39, no. 3, pp. 383-390. https://doi.org/10.1007/s10545-015-9912-y

Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study. / Gelder, Carin; Poelman, Esther; Plug, Iris et al.
In: Journal of Inherited Metabolic Disease, Vol. 39, No. 3, 2016, p. 383-390.

Research output: Contribution to journal › Article › Academic › peer-review

TY - JOUR

T1 - Effects of a higher dose of alglucosidase alfa on ventilator-free survival and motor outcome in classic infantile Pompe disease: an open-label single-center study

AU - Gelder, Carin

AU - Poelman, Esther

AU - Plug, Iris

AU - Hoogeveen - Westerveld, Marianne

AU - van der Beek, N.A.M.E.

AU - Reuser, Arnold

AU - van der Ploeg, Ans

PY - 2016

Y1 - 2016

U2 - 10.1007/s10545-015-9912-y

DO - 10.1007/s10545-015-9912-y

M3 - Article

C2 - 26768149

SN - 0141-8955

VL - 39

SP - 383

EP - 390

JO - Journal of Inherited Metabolic Disease

JF - Journal of Inherited Metabolic Disease

IS - 3

ER -