Effects of higher and more frequent dosing of alglucosidase alfa and immunomodulation on long-term clinical outcome of classic infantile Pompe patients

Research output: Contribution to journalArticleAcademicpeer-review

25 Citations (Scopus)
56 Downloads (Pure)
Original languageEnglish
Pages (from-to)1243-1253
Number of pages11
JournalJournal of Inherited Metabolic Disease
Volume43
Issue number6
DOIs
Publication statusPublished - 2020

Research programs

  • EMC MM-01-54-01
  • EMC MM-04-44-02

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