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Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation

  • V Capo
  • , MC Castiello
  • , E Fontana
  • , S Penna
  • , M Bosticardo
  • , E Draghici
  • , LP Poliani
  • , LS Sergi
  • , R Rigoni
  • , B Cassani
  • , M Zanussi
  • , P Carrera
  • , P Uva
  • , K Dobbs
  • , N Sacchetti
  • , LD Notarangelo
  • , Niek Til
  • , Gerard Wagemaker
  • , A Villa

Research output: Contribution to journalArticleAcademicpeer-review

26 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)928-941.e8
JournalJournal of Allergy and Clinical Immunology
Volume142
Issue number3
DOIs
Publication statusPublished - 2018

Research programs

  • EMC OR-01

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