Enzyme replacement therapy in late-onset Pompe's disease: a three-year follow-up

Leon Winkel, Hannerieke van den Hout, Jozef Kamphoven, JAM (Jeroen) Disseldorp, M Remmerswaal, WFM Arts, MCB (Christa) Loonen, Arnold Vulto, Pieter van Doorn, G (Gerard) de Jong, Hop, GPA Smit, SK Shapira, MA den Boer, Otto Diggelen, Arnold Reuser, Ans van der Ploeg

Research output: Contribution to journalArticleAcademicpeer-review

213 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)495-502
Number of pages8
JournalAnnals of Neurology
Volume55
DOIs
Publication statusPublished - 2004

Research programs

  • EMC MGC-02-96-01
  • EMC MM-01-39-06-A
  • EMC MM-01-54-01
  • EMC MM-04-44-02
  • EMC NIHES-01-64-03
  • EMC OR-01-34-01

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