Enzyme replacement therapy reduces the risk for wheelchair dependency in adult Pompe patients

Research output: Contribution to journalArticleAcademicpeer-review

14 Citations (Scopus)
10 Downloads (Pure)
Original languageUndefined/Unknown
Article number82
JournalOrphanet Journal of Rare Diseases
Volume13
DOIs
Publication statusPublished - 2018

Research programs

  • EMC MM-01-54-01

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