Etranacogene dezaparvovec (AMT-061 phase 2b): normal/near normal FIX activity and bleed cessation in hemophilia B

A Von Drygalski, A Giermasz, G Castaman, NS Key, S Lattimore, Frank Leebeek, W Miesbach, M Recht, A Long, R Gut, EK Sawyer, SW Pipe

Research output: Contribution to journalArticleAcademicpeer-review

76 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)3241-3247
Number of pages7
JournalBlood advances
Issue number21
Publication statusPublished - 2019

Research programs

  • EMC COEUR-09

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