European consensus for starting and stopping enzyme replacement therapy in adult patients with Pompe disease: A 10-year experience

Ans van der Ploeg, ME Kruijshaar, A Toscano, P Laforet, C Angelini, RHL Lachmann, SIP Pascual, Pim Pijnappel, N.A.M.E. van der Beek, M Roberts, K Rosler, T Stulnig, Pieter van Doorn, PYK Van den Bergh, J Vissing, B Schoser

Research output: Contribution to journalArticleAcademic

57 Downloads (Pure)
Original languageUndefined/Unknown
Pages (from-to)19-34
Number of pages16
JournalNervno-Myshechnye Bolezni
Volume8
Issue number4
DOIs
Publication statusPublished - 2018

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