Impact of enzyme replacement therapy on survival in adults with Pompe disease: results from a prospective international observational study

Deniz Gungor, Michelle Kruijshaar, I (Iris) Plug, RB D'Agostino, Marloes Hagemans, Pieter van Doorn, Arnold Reuser, Ans van der Ploeg

Research output: Contribution to journalArticleAcademicpeer-review

91 Citations (Scopus)
17 Downloads (Pure)
Original languageUndefined/Unknown
JournalOrphanet Journal of Rare Diseases
Volume8
DOIs
Publication statusPublished - 2013

Research programs

  • EMC MGC-02-96-01
  • EMC MM-01-54-01
  • EMC MM-04-44-02

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