Interim analysis: Open-label extension study of leniolisib for patients with APDS

V. Koneti Rao*, Elaine Kulm, Anna Šedivá, Alessandro Plebani, Catharina Schuetz, Anna Shcherbina, Virgil A. Dalm, Antonino Trizzino, Yulia Zharankova, Sharon Webster, Alanvin Orpia, Julia Körholz, Vassilios Lougaris, Yulia Rodina, Kath Radford, Jason Bradt, Anurag Relan, Steven M. Holland, Michael J. Lenardo, Gulbu Uzel

*Corresponding author for this work

Research output: Contribution to journalArticleAcademicpeer-review

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Medicine and Dentistry

Pharmacology, Toxicology and Pharmaceutical Science