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Large variation in effects during 10 years of enzyme therapy in adults with Pompe disease

Research output: Contribution to journalArticleAcademicpeer-review

126 Citations (Scopus)
Original languageUndefined/Unknown
Article numbere1756-e1767
JournalNeurology
Volume93
Issue number19
Publication statusPublished - 2019

Research programs

  • EMC MM-01-54-01

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