Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease

Merel Stok; Helen Boer; MW Huston; EH Jacobs; Onno Roovers; Trui Visser; Holger Jahr; Dirk-jan Duncker; Elza Deel; Arnold Reuser; Niek Til; Gerard Wagemaker

doi:10.1016/j.omtm.2020.04.023

Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease

Merel Stok, Helen Boer, MW Huston, EH Jacobs, Onno Roovers, Trui Visser, Holger Jahr, Dirk-jan Duncker, Elza Deel, Arnold Reuser, Niek Til, Gerard Wagemaker

Research output: Contribution to journal › Article › Academic › peer-review

30 Citations (Scopus)

39 Downloads (Pure)

Original language	English
Pages (from-to)	1014-1025
Number of pages	12
Journal	Molecular Therapy-Methods & Clinical Development
Volume	17
DOIs	https://doi.org/10.1016/j.omtm.2020.04.023
Publication status	Published - 2020

Research programs

EMC MGC-01-12-03
EMC OR-01
EMC MM-01-54-01

Access to Document

10.1016/j.omtm.2020.04.023

Repub_127067_O-A.pdfFinal published version, 2.36 MB

http://hdl.handle.net/1765/127067

Cite this

@article{5ba2d573e287469e8598bd04ea4234f2,

title = "Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease",

author = "Merel Stok and Helen Boer and MW Huston and EH Jacobs and Onno Roovers and Trui Visser and Holger Jahr and Dirk-jan Duncker and Elza Deel and Arnold Reuser and Niek Til and Gerard Wagemaker",

year = "2020",

doi = "10.1016/j.omtm.2020.04.023",

language = "English",

volume = "17",

pages = "1014--1025",

journal = "Molecular Therapy-Methods & Clinical Development",

issn = "2329-0501",

publisher = "Cell Press",

}

TY - JOUR

T1 - Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease

AU - Stok, Merel

AU - Boer, Helen

AU - Huston, MW

AU - Jacobs, EH

AU - Roovers, Onno

AU - Visser, Trui

AU - Jahr, Holger

AU - Duncker, Dirk-jan

AU - Deel, Elza

AU - Reuser, Arnold

AU - Til, Niek

AU - Wagemaker, Gerard

PY - 2020

Y1 - 2020

U2 - 10.1016/j.omtm.2020.04.023

DO - 10.1016/j.omtm.2020.04.023

M3 - Article

C2 - 32462050

SN - 2329-0501

VL - 17

SP - 1014

EP - 1025

JO - Molecular Therapy-Methods & Clinical Development

JF - Molecular Therapy-Methods & Clinical Development

ER -