Original language | English |
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Pages (from-to) | 1014-1025 |
Number of pages | 12 |
Journal | Molecular Therapy-Methods & Clinical Development |
Volume | 17 |
DOIs | |
Publication status | Published - 2020 |
Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease
Merel Stok, Helen Boer, MW Huston, EH Jacobs, Onno Roovers, Trui Visser, Holger Jahr, Dirk-jan Duncker, Elza Deel, Arnold Reuser, Niek Til, Gerard Wagemaker
Research output: Contribution to journal › Article › Academic › peer-review
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