Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease

Merel Stok, Helen Boer, MW Huston, EH Jacobs, Onno Roovers, Trui Visser, Holger Jahr, Dirk-jan Duncker, Elza Deel, Arnold Reuser, Niek Til, Gerard Wagemaker

Research output: Contribution to journalArticleAcademicpeer-review

19 Citations (Scopus)
7 Downloads (Pure)
Original languageEnglish
Pages (from-to)1014-1025
Number of pages12
JournalMolecular Therapy-Methods & Clinical Development
Publication statusPublished - 2020

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