Lentiviral Stem Cell Gene Therapy for Pompe Disease

Qiushi Liang, Merel Stok, Yvette van Helsdingen, Guus van der Velden, Ed Jacobs, Dirk Duncker, Arnold Reuser, Ans van der Ploeg, Arnold Vulto, Niek P van Til, Gerard Wagemaker*

*Corresponding author for this work

Research output: Contribution to journalArticleAcademicpeer-review

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Original languageEnglish
Pages (from-to)S64
JournalJournal of Neuromuscular Diseases
Issue numbers1
Publication statusPublished - 2015

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