Long-term benefit of enzyme replacement therapy in Pompe disease A 5-year prospective study

Research output: Contribution to journalArticleAcademicpeer-review

100 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)2365-2373
Number of pages9
JournalNeurology
Volume89
Issue number23
DOIs
Publication statusPublished - 2017

Research programs

  • EMC MM-01-54-01

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