@article{01a4e2508ad74d9ea98f3487d4ef8fac,
title = "Long-term benefit of enzyme replacement therapy in Pompe disease A 5-year prospective study",
author = "Esther Kuperus and Michelle Kruijshaar and Stephan Wens and \{de Vries\}, Juna and Marein Favejee and Chris Meijden and Dimitris Rizopoulos and Esther Brusse and \{van Doorn\}, Pieter and \{van der Ploeg\}, Ans and \{van der Beek\}, N.A.M.E.",
year = "2017",
doi = "10.1212/wnl.0000000000004711",
language = "Undefined/Unknown",
volume = "89",
pages = "2365--2373",
journal = "Neurology",
issn = "0028-3878",
publisher = "Lippincott Williams \& Wilkins",
number = "23",
}