Long-term treatment effect in cerebrotendinous xanthomatosis depends on age at treatment start

BML Stelten, Hidde Huidekoper, BP van De Warrenburg, EH Brilstra, CEM Hollak, HR Haak, LAJ Kluijtmans, RA Wevers, A Verrips

Research output: Contribution to journalArticleAcademicpeer-review

81 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)E83-E95
JournalNeurology
Volume92
Issue number2
DOIs
Publication statusPublished - 2019

Research programs

  • EMC MM-01-54-01

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