Open-label extension study following the Late-Onset Treatment Study (LOTS) of alglucosidase alfa

Ans van der Ploeg, RJ Barohn, L Carlson, J Charrow, PR Clemens, RJ Hopkin, PS Kishnani, P Laforet, C Morgan, S Nations, A Pestronk, H Plotkin, B Rosenbloom, K Sims, E Tsao

Research output: Contribution to journalArticleAcademicpeer-review

103 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)456-461
Number of pages6
JournalMolecular Genetics and Metabolism
Volume107
DOIs
Publication statusPublished - 2012

Research programs

  • EMC MM-01-54-01

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