Outcome measures for children with mitochondrial disease: consensus recommendations for future studies from a Delphi-based international workshop

S Koene, L van Bon, E Bertini, C Jimenez-Moreno, Lianne van der Giessen, IB Groot, R McFarland, S Parikh, S Rahman, M Wood, J Zeman, A Janssen, J Smeitink

Research output: Contribution to journalArticleAcademicpeer-review

25 Citations (Scopus)
16 Downloads (Pure)
Original languageUndefined/Unknown
Pages (from-to)1267-1273
Number of pages7
JournalJournal of Inherited Metabolic Disease
Volume41
Issue number6
DOIs
Publication statusPublished - 2018

Research programs

  • EMC MM-01-54-01

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