Pathway to diagnosis and burden of illness in mucopolysaccharidosis type VII - a European caregiver survey

A Morrison, Esmeralda Oussoren, T Friedel, J Cruz, N Yilmaz

Research output: Contribution to journalArticleAcademicpeer-review

18 Citations (Scopus)
6 Downloads (Pure)
Original languageUndefined/Unknown
Article number254
JournalOrphanet Journal of Rare Diseases
Volume14
Issue number1
DOIs
Publication statusPublished - 2019

Research programs

  • EMC MM-01-54-01

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