Phase 3 Trial of RNAi Therapeutic Givosiran for Acute Intermittent Porphyria

M Balwani, E Sardh, P Ventura, PA Peiro, DC Rees, U Stolzel, DM Bissell, HL Bonkovsky, J Windyga, KE Anderson, C Parker, SM Silver, SB Keel, JD Wang, PE Stein, P Harper, D Vassiliou, B Wang, J Phillips, A IvanovaJanneke Langendonk, R Kauppinen, E Minder, Y Horie, C Penz, JH Chen, SB Liu, JJ Ko, MT Sweetser, P Garg, A Vaishnaw, JB Kim, AR Simon, L Gouya

Research output: Contribution to journalArticleAcademicpeer-review

218 Citations (Scopus)
Original languageEnglish
Pages (from-to)2289-2301
Number of pages13
JournalNew England Journal of Medicine
Issue number24
Publication statusPublished - 2020

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