Phosphodiesterase-5 Inhibition and Alzheimer's Disease Risk: A Mendelian Randomisation Study

  • Marta Alcalde-Herraiz
  • , Benjamin Woolf
  • , Junqing Xie
  • , Emma Anderson
  • , Dipender Gill
  • , Ioanna Tzoulaki
  • , Laura M. Winchester
  • , James Yarmolinsky
  • , Daniel Prieto-Alhambra*
  • , Danielle Newby
  • *Corresponding author for this work

Research output: Contribution to journalArticleAcademicpeer-review

Abstract

While preclinical studies suggest that Phosphodiesterase 5 (PDE5) inhibition may reduce cognitive impairment, findings from observational studies on whether PDE5 inhibitors reduce Alzheimer's disease (AD) risk have been inconsistent. We performed a two-sample cis-Mendelian Randomisation (MR) analysis to estimate the causal effect of PDE5 inhibition on AD risk. The analysis was performed across four different genome-wide association studies (GWAS) of AD to enhance reliability through triangulation. Additionally, a sex-stratified MR analysis using data from UK Biobank was performed to assess potential sex-specific effects. No evidence of a causal association between PDE5 inhibition and AD risk was found in the main analyses. Similar findings were obtained in the sex-stratified analysis. Our study uses genetic data to triangulate the evidence and suggests that PDE5 inhibitors are unlikely to decrease the risk of AD. Further research is needed to thoroughly understand the impact of PDE5 inhibitors on the risk of Alzheimer's disease.

Original languageEnglish
Article numbere70265
JournalAging Cell
Volume24
Issue number12
DOIs
Publication statusPublished - Dec 2025

Bibliographical note

Publisher Copyright:
© 2025 The Author(s). Aging Cell published by Anatomical Society and John Wiley & Sons Ltd.

Fingerprint

Dive into the research topics of 'Phosphodiesterase-5 Inhibition and Alzheimer's Disease Risk: A Mendelian Randomisation Study'. Together they form a unique fingerprint.

Cite this