Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE

Rana Yadak, R Cabrera-Perez, J Torres-Torronteras, M Bugiani, Joost Haeck, MW Huston, Elly Taal, S Goffart, Ed Jacobs, M Stok, L Leonardelli, L Biasco, Rob Verdijk, Monique Bernsen, GJG Ruijter, R Marti, G Wagemaker, NP Til, IFM Coo

Research output: Contribution to journalArticleAcademicpeer-review

16 Citations (Scopus)
15 Downloads (Pure)
Original languageUndefined/Unknown
Pages (from-to)152-165
Number of pages14
JournalMolecular Therapy-Methods & Clinical Development
Publication statusPublished - 2018

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