@article{a66c5ce72407402c9dfd4a301b27fbe8,
title = "Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE",
author = "Rana Yadak and R Cabrera-Perez and J Torres-Torronteras and M Bugiani and Joost Haeck and MW Huston and Elly Taal and S Goffart and Ed Jacobs and M Stok and L Leonardelli and L Biasco and Rob Verdijk and Monique Bernsen and GJG Ruijter and R Marti and G Wagemaker and NP Til and IFM Coo",
year = "2018",
doi = "10.1016/j.omtm.2018.01.001",
language = "Undefined/Unknown",
volume = "8",
pages = "152--165",
journal = "Molecular Therapy-Methods \& Clinical Development",
issn = "2329-0501",
publisher = "Cell Press",
}