Prime editing for functional repair in patient-derived disease models

IF Schene, IP Joore, R Oka, M Mokry, AHM van Vugt, R van Boxtel, HPJ van der Doef, Luc van der Laan, Monique Verstegen, PM van Hasselt, EES Nieuwenhuis, SA Fuchs

Research output: Contribution to journalArticleAcademicpeer-review

163 Citations (Scopus)
82 Downloads (Pure)
Original languageEnglish
Article number5352
JournalNature Communications
Volume11
Issue number1
DOIs
Publication statusPublished - 2020

Research programs

  • EMC OR-01

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