rAAV-CFTRAR Rescues the Cystic Fibrosis Phenotype in Human Intestinal Organoids and Cystic Fibrosis Mice

D Vidovic, MS Carlon, MF da Cunha, JF Dekkers, MI Hollenhorst, Marcel Bijvelds, AS Ramalho, C Van den Haute, M Ferrante, V Baekelandt, Hettie Janssens, K de Boeck, I Sermet-Gaudelus, Hugo de Jonge, R Gijsbers, JM Beekman, A Edelman, Z Debyser

Research output: Contribution to journalArticleAcademicpeer-review

51 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)288-298
Number of pages11
JournalAmerican Journal of Respiratory and Critical Care Medicine
Volume193
Issue number3
DOIs
Publication statusPublished - 2016

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