Respiratory function during enzyme replacement therapy in late-onset Pompe disease: longitudinal course, prognostic factors, and the impact of time from diagnosis to treatment start

DW Stockton, P Kishnani, Ans van der Ploeg, J, Jr Llerena, M Boentert, M Roberts, BJ Byrne, R Araujo, S S Maruti, N Thibault, K Verhulst, KI Berger

Research output: Contribution to journalArticleAcademicpeer-review

11 Citations (Scopus)
3 Downloads (Pure)
Original languageEnglish
Pages (from-to)3038-3053
Number of pages16
JournalJournal of Neurology
Issue number10
Publication statusPublished - 2020

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