@article{29f5f8a9590a42b4ab5d9ba0550a3138,
title = "Succesful treatment of UGT1A1 deficiency in a rat model of Crigler-Najjar disease by intravenous administration of a liver-specific lentiviral vector",
author = "\{van der Wegen\}, \{CG (Pascal)\} and Rogier Louwen and Ali Imam and Luna Offerman and Sinaasappel, \{M (Maarten)\} and Frank Grosveld and Bob Scholte",
year = "2006",
language = "Undefined/Unknown",
volume = "12",
pages = "374--381",
journal = "Molecular Therapy",
issn = "1525-0016",
publisher = "Cell Press",
number = "2",
}