Survival and associated factors in 268 adults with Pompe disease prior to treatment with enzyme replacement therapy

Deniz Gungor, J de Vries, Hop, Arnold Reuser, Pieter van Doorn, Ans van der Ploeg, Marloes Hagemans

Research output: Contribution to journalArticleAcademicpeer-review

86 Citations (Scopus)
15 Downloads (Pure)
Original languageUndefined/Unknown
Pages (from-to)34
JournalOrphanet Journal of Rare Diseases
Volume6
DOIs
Publication statusPublished - 2011

Research programs

  • EMC MGC-02-96-01
  • EMC MM-01-54-01
  • EMC MM-04-44-02
  • EMC NIHES-01-66-01

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