Ten years of the international Pompe survey: patient reported outcomes as a reliable tool for studying treated and untreated children and adults with non-classic Pompe disease

Chris Meijden, Deniz Gungor, Michelle Kruijshaar, ADJ Muir, HA Broekgaarden, Ans van der Ploeg

Research output: Contribution to journalArticleAcademicpeer-review

27 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)495-503
Number of pages9
JournalJournal of Inherited Metabolic Disease
Volume38
Issue number3
DOIs
Publication statusPublished - 2015

Research programs

  • EMC MM-01-54-01

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