Transatlantic combined and comparative data analysis of 1095 patients with urea cycle disordersA successful strategy for clinical research of rare diseases

R Posset, SF Garbade, N Boy, AB Burlina, C Dionisi-Vici, D Dobbelaere, Monique Williams, J Zeman

Research output: Contribution to journalArticleAcademicpeer-review

34 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)93-106
Number of pages14
JournalJournal of Inherited Metabolic Disease
Issue number1
Publication statusPublished - 2019

Research programs

  • EMC MM-01-54-01

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