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Early umbilical cord blood-derived stem cell transplantation does not prevent neurological deterioration in mucopolysaccharidosis type III

  • L Welling
  • , JP Marchal
  • , P van Hasselt
  • , Ans van der Ploeg
  • , FA Wijburg
  • , JJ Boelens

Research output: Contribution to journalArticleAcademicpeer-review

44 Citations (Scopus)
Original languageUndefined/Unknown
Pages (from-to)63-68
Number of pages6
JournalJournal of Inherited Metabolic Disease
Volume18
Publication statusPublished - 2015

Research programs

  • EMC MM-01-54-01

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